REGENXBIO INC.;REGENTS OF THE UNIVERSITY OF MINNESOTA
发明人:
MCIVOR, R., Scott RS,BELUR, Lalitha R. LR,LOW, Walter W,FAIRBANKS, Carolyn C,KOZARSKY, Karen K,.麥基弗,.貝勒,.洛,.費爾班克斯,.科扎爾斯基
申请号：
HK16110439.0
公开号：
HK1222093A
申请日:
2016.09.01
申请国别(地区):
HK
年份:
2017
代理人:
摘要：
A method to prevent, inhibit or treat one or more symptoms associated with a disease of the central nervous system by intrathecally, intracerebroventricularly or endovascularly administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease.
