MCIVOR, R., Scott,BELUR, Lalitha R.,LOW, Walter,FAIRBANKS, Carolyn,KOZARSKY, Karen
申请号:
HK16111030.1
公开号:
HK1222767A
申请日:
2016.09.20
申请国别(地区):
HK
年份:
2017
代理人:
摘要:
A method to prevent, inhibit or treat one or more symptoms associated with a disease of the central nervous system by intrathecally, intracerebroventricularly or endovascularly administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease.