Regents of the University of Minnesota;REGENXBIO Inc.
发明人:
R. Scott McIvor,Lalitha R. Belur,Walter Low,Carolyn Fairbanks,Karen Kozarsky
申请号：
US15987490
公开号：
US20180264090A1
申请日:
2018.05.23
申请国别(地区):
US
年份:
2018
代理人:
摘要：
A method to prevent, inhibit or treat one or more symptoms associated with a disease of the central nervous system by intrathecally, intracerebroventricularly or endovascularly administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease.
