REGENXBIO Inc.;Regents of the University of Minnesota
发明人:
McIvor, R. Scott,Belur, Lalitha R.,Low, Walter,Fairbanks, Carolyn,Kozarsky, Karen
申请号:
AU2014265417
公开号:
AU2014265417A1
申请日:
2014.05.15
申请国别(地区):
AU
年份:
2015
代理人:
摘要:
A method to prevent, inhibit or treat one or more symptoms associated with a disease of the central nervous system by intrathecally, intracerebroventricularly or endovascularly administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease.