REGENTS OF THE UNIVERSITY OF MINNESOTA;REGENXBIO INC.;REGENXBIO INC.;銳進科斯生物股份有限公司
发明人:
MCIVOR, R. Scott,BELUR, Lalitha R.,KOZARSKY, Karen,L‧R‧貝勒,KOZARSKY, Karen,K‧科扎爾斯基
申请号：
HK18115428
公开号：
HK1256341A1
申请日:
2018.12.03
申请国别(地区):
HK
年份:
2019
代理人:
摘要：
A method to prevent, inhibit or treat one or more symptoms associated with disease of the central nervous system by intranasally, intrathecally, intracerebrovascularly or intravenously administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease, in an amount effective, e.g., to provide for cross-correction.
