McIvor, R. Scott,Belur, Lalitha R.,Kozarsky, Karen
申请号:
AU2016263119
公开号:
AU2016263119A1
申请日:
2016.05.13
申请国别(地区):
AU
年份:
2018
代理人:
摘要:
A method to prevent, inhibit or treat one or more symptoms associated with disease of the central nervous system by intranasally, intrathecally, intracerebrovascularly or intravenously administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease, in an amount effective, e.g., to provide for cross-correction.