Regents of the University of Minnesota;REGENXBIO Inc.
发明人:
R. Scott McIvor,Lalitha R. Belur,Karen Kozarsky
申请号：
US15813908
公开号：
US20180071373A1
申请日:
2017.11.15
申请国别(地区):
US
年份:
2018
代理人:
摘要：
A method to prevent, inhibit or treat one or more symptoms associated with disease of the central nervous system by intranasally, intrathecally, intracerebrovascularly or intravenously administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease, in an amount effective, e.g., to provide for cross-correction.
