Maria Joann Denaro,Mitchell Howard Finer,Gabor Veres,Julian Down
申请号:
US14488058
公开号:
US09061031B2
申请日:
2014.09.16
申请国别(地区):
US
年份:
2015
代理人:
摘要:
The present invention provides compositions comprising retroviral vectors, transduced cells, and methods of using the same for gene therapy. In particular, the present invention relates to lentiviral vectors and cells transduced with those vectors to provide gene therapy to subjects having an adrenoleukodystrophy and/or adrenomyeloneuropathy.