DENARO MARIA JOANN,FINER MITCHELL HOWARD,VERES GABOR
申请号:
IN2335/MUMNP/2013
公开号:
IN2013MN02335A
申请日:
2013.12.12
申请国别(地区):
IN
年份:
2014
代理人:
摘要:
The present invention provides compositions ccomprising retroviral vectors transduced cells and methods of using the same for gene therapy. In particular the present invention relates to lentiviral vectors and cells transduced with those vectors to provide gene therapy to subjects having an adrenoleukodystrophy and/or adrenomyeloneuropathy.