Maria Joann Denaro;Mitchell Howard Finer;Gabor Veres
发明人:
Maria Joann Denaro,Mitchell Howard Finer,Gabor Veres
申请号：
US13492553
公开号：
US20130004471A1
申请日:
2012.06.08
申请国别(地区):
US
年份:
2013
代理人:
摘要：
The present invention provides compositions comprising retroviral vectors, transduced cells, and methods of using the same for gene therapy. In particular, the present invention relates to lentiviral vectors and cells transduced with those vectors to provide gene therapy to subjects having an adrenoleukodystrophy and/or adrenomyeloneuropathy.
