Denaro, Maria Joann,Finer, Mitchell Howard,Veres, Gabor
申请号:
AU2012267512
公开号:
AU2012267512B2
申请日:
2012.06.08
申请国别(地区):
AU
年份:
2014
代理人:
摘要:
The present invention provides compositions ccomprising retroviral vectors, transduced cells, and methods of using the same for gene therapy. In particular, the present invention relates to lentiviral vectors and cells transduced with those vectors to provide gene therapy to subjects having an adrenoleukodystrophy and/or adrenomyeloneuropathy.