Ante Sven Lundberg,Samarth Kulkarni,Lawrence Klein,Hari Kumar Padmanabhan
申请号：
US16315540
公开号：
US20190224340A1
申请日:
2017.07.06
申请国别(地区):
US
年份:
2019
代理人:
摘要：
The present application provides materials and methods for treating a patient with one or more conditions associated with SCN10A whether ex vivo or in vivo. In addition, the present application provides materials and methods for editing and/or modulating the expression of SCN10A gene in a cell by genome editing.
