Kabadi, Ami Meda,Cowan, Chad Albert,Lundberg, Ante Sven
申请号：
AU2016344609
公开号：
AU2016344609A1
申请日:
2016.10.28
申请国别(地区):
AU
年份:
2018
代理人:
摘要：
The present application provides materials and methods for treating a patient with Duchenne Muscular Dystrophy (DMD) both ex vivo and in vivo. In addition, the present application provides materials and methods for editing a dystrophin gene in a cell by genome editing.
