Ami Meda KABADI,Chad Albert COWAN,Ante Sven LUNDBERG
申请号：
US15763328
公开号：
US20190374655A1
申请日:
2016.10.28
申请国别(地区):
US
年份:
2019
代理人:
摘要：
The present application provides materials and methods for treating a patient with Duchenne Muscular Dystrophy (DMD) both ex vivo and in vivo. In addition, the present application provides materials and methods for editing a dystrophin gene in a cell by genome editing.
