Ante Sven LUNDBERG,Samarth KULKARNI,Lawrence KLEIN,Yvonne Sarah ARATYN,Roman Lvovitch BOGORAD,Hari Kumar PADMANABHAN
申请号：
US16488149
公开号：
US20200248168A1
申请日:
2018.02.15
申请国别(地区):
US
年份:
2020
代理人:
摘要：
The present application provides materials and methods for treating a patient with one or more conditions associated with PCSK9 whether ex vivo or in vivo. In addition, the present application provides materials and methods for editing and/or modulating the expression of PCSK9 gene in a cell by genome editing.
