Ante Sven LUNDBERG,Samarth KULKARNI,Lawrence KLEIN,Hari Kumar PADMANABHAN
申请号：
US16312651
公开号：
US20190211362A1
申请日:
2017.06.27
申请国别(地区):
US
年份:
2019
代理人:
摘要：
The present application provides materials and methods for treating a patient with one or more conditions associated with DMPK whether ex vivo or in vivo. In addition, the present application provides materials and methods for editing and/or modulating the expression of DMPK gene in a cell by genome editing.
