LUNDBERG, ANTE SVEN,KULKARNI, SAMARTH,KLEIN, LAWRENCE,PADMANABHAN, HARI KUMAR
申请号：
CA3029119
公开号：
CA3029119A1
申请日:
2017.06.22
申请国别(地区):
CA
年份:
2018
代理人:
摘要：
The present application provides materials and methods for treating a patient with one or more condition associated with FXN whether ex vivo or in vivo. In addition, the present application provides materials and methods for editing and/or modulating the expression of FXN gene in a cell by genome editing.
