DENARO, MARIA JOANN,FINER, MITCHELL HOWARD,VERES, GABOR
申请号:
CA2838749
公开号:
CA2838749A1
申请日:
2012.06.08
申请国别(地区):
CA
年份:
2012
代理人:
摘要:
The present invention provides compositions ccomprising retroviral vectors, transduced cells, and methods of using the same for gene therapy. In particular, the present invention relates to lentiviral vectors and cells transduced with those vectors to provide gene therapy to subjects having an adrenoleukodystrophy and/or adrenomyeloneuropathy.