INSTITUT NATIONAL DE LA SANTE ET DE LA RECHERCHE MEDICALE - INSERM;Université de Paris;Fondation Imagine;ASSISTANCE PUBLIQUE, HOPITAUX DE PARIS
发明人:
申请号：
EP20168215.0
公开号：
EP3702461A1
申请日:
2014.07.08
申请国别(地区):
EP
年份:
2020
代理人:
摘要：
The present invention relates to methods for performing antisense oligonucleotide-mediated exon skipping in the retina of a subject in need thereof. In particular, the present invention relates to a method for performing antisense oligonucleotide-mediated exon skipping in a retina cell of a subject comprising the step of injecting into the vitreous of the subject an amount of the antisense oligonucleotide.
