GUILD Braydon Charles,DEROSA Frank,HEARTLEIN Michael,CONCINO Michael
申请号：
SI201031681
公开号：
SI2506857T1
申请日:
2010.11.30
申请国别(地区):
SI
年份:
2018
代理人:
摘要：
Disclosed herein are compositions and methods of modulating the expression of gene or the production of a protein by transfecting target cells with nucleic acids. The compositions disclosed herein demonstrate a high transfection efficacy and are capable of ameliorating diseases associated with protein or enzyme deficiencies.
