Guild, Braydon Charles,Derosa, Frank,Heartlein, Michael,Concino, Michael
申请号：
HRP20180696
公开号：
HRP20180696T1
申请日:
2018.05.03
申请国别(地区):
HR
年份:
2018
代理人:
摘要：
Disclosed herein are compositions and methods of modulating the expression of gene or the production of a protein by transfecting target cells with nucleic acids. The compositions disclosed herein demonstrate a high transfection efficacy and are capable of ameliorating diseases associated with protein or enzyme deficiencies.
