GUILD, Braydon,DEROSA, Frank,HEARTLEIN, Michael,CONCINO, Michael
申请号：
HUE10835016
公开号：
HUE038039T2
申请日:
2010.11.30
申请国别(地区):
HU
年份:
2018
代理人:
摘要：
Disclosed herein are compositions and methods of modulating the expression of gene or the production of a protein by transfecting target cells with nucleic acids. The compositions disclosed herein demonstrate a high transfection efficacy and are capable of ameliorating diseases associated with protein or enzyme deficiencies.
