UTILISATION DE LIPASE ACIDE LYSOSOMALE POUR LE TRAITEMENT DE LA DÉFICIENCE EN LIPASE ACIDE LYSOSOMALE CHEZ DES PATIENTS

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专利权人:

Alexion Pharmaceuticals; Inc.

发明人:

申请号：

EP19199414.4

公开号：

EP3650039A1

申请日:

2011.09.09

申请国别(地区):

EP

年份:

2020

代理人:

摘要：

The present invention provides treating LAL deficiency (e.g. Wolman's disease, CESD) comprising administering to a mammal a therapeutically effective amount of lysosomal acid lipsase with an effective dosage frequency. Methods of improving growth and liver function, increasing LAL tissue concentration, and increasing LAL activity in a human patient suffering from LAL deficiency are also provided.

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中国工程科技知识中心

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