Dias, Anusha,Abysalh, Jonathan,Bettencourt, Brian,Derosa, Frank,Heartlein, Michael
申请号：
AU2018224326
公开号：
AU2018224326A1
申请日:
2018.02.27
申请国别(地区):
AU
年份:
2019
代理人:
摘要：
The present invention provides, among other things, improved methods and pharmaceutical compositions for treating cystic fibrosis based on codon optimized mRNA encoding a Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) protein.
