DIAS, ANUSHA,ABYSALH, JONATHAN,BETTENCOURT, BRIAN,DEROSA, FRANK,HEARTLEIN, MICHAEL
申请号：
CA3054062
公开号：
CA3054062A1
申请日:
2018.02.27
申请国别(地区):
CA
年份:
2018
代理人:
摘要：
The present invention provides, among other things, improved methods and pharmaceutical compositions for treating cystic fibrosis based on codon optimized mRNA encoding a Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) protein.
