AAV-IDUA VECTOR FOR TREATMENT OF ASSOCIATED WITH MPS I BLINDINGS
- 专利权人:
- 发明人:
- 申请号：
- RU2018132517
- 公开号：
- RU2018132517A3
- 申请日:
- 申请国别(地区):
- RU
- 年份:
- 2020
- 代理人:
- 摘要：
- This invention relates to viral vectors for delivery of alpha-L-iduronidase to the cornea of a subject and methods of using the same for treatment and prevention of corneal clouding and blindness in a subject due to mucopolysaccharidosis I.
- 来源网站：
- 中国工程科技知识中心
相关发明人
相关专利
- AAV-IDUA vector for treatment of MPS I-associated blindness
- AAV-IDUA VECTOR FOR TREATMENT OF MPS I-ASSOCIATED BLINDNESS
- Capsid-free AAV vectors, compositions, and methods for vector production and gene delivery
- MODIFIED AAV CONSTRUCTS AND USES THEREOF
- Recombinant Adeno-Associated virus (AAV) vector particles displaying high-affinity ligands for cell-type specific gene delivery
