AAV-IDUA vector for treatment of MPS I-associated blindness

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专利权人:

The University of North Carolina at Chapel Hill

发明人:

Hirsch, Matthew Louis,Samulski, Richard Jude

申请号：

AU2017223465

公开号：

AU2017223465A1

申请日:

2017.02.22

申请国别(地区):

AU

年份:

2018

代理人:

摘要：

This invention relates to viral vectors for delivery of alpha-L-iduronidase to the cornea of a subject and methods of using the same for treatment and prevention of corneal clouding and blindness in a subject due to mucopolysaccharidosis I.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/