COMPOSITIONS ET PROCÉDÉS DE MODULATION DE L'EXPRESSION DE LA FRATAXINE
- 专利权人:
- Rana Therapeutics; Inc.
- 发明人:
- 申请号：
- EP14836374.0
- 公开号：
- EP3033425A4
- 申请日:
- 2014.08.15
- 申请国别(地区):
- EP
- 年份:
- 2017
- 代理人:
- 摘要：
- Provided herein are compositions and methods for increasing Frataxin (FXN) expression. Compositions and methods for treating Friedrich's ataxia are also provided.
- 来源网站：
- 中国工程科技知识中心
相关发明人
相关专利
- Use of erythropoietin for the treatment of Friedreich's ataxia
- modified friedreich ataxia genes and vectors for gene therapy
- MODIFIED ATAXIA FREEDREICH GENES AND VECTORS FOR GENE THERAPY
- Genes of Friedreich's ataxia and modified vectors for gene therapy
- COMPOSITIONS AND METHODS FOR MODULATING EXPRESSION OF FRATAXIN
