DE KIMPE, JOSEPHUS JOHANNES,PLATENBURG, GERARDUS JOHANNES,VAN DEUTEKOM, JUDITH CHRISTINA THEODORA,AARTSMA-RUS, ANNEMIEKE,VAN OMMEN, GARRIT-JAN BOUDEWIJN
申请号：
DK13160338
公开号：
DK2607484T3
申请日:
2009.01.13
申请国别(地区):
DK
年份:
2016
代理人:
摘要：
The invention relates to a method for inducing or promoting skipping of exon 45 of DMD pre-mRNA in a Duchenne Muscular Dystrophy patient, preferably in an isolated (muscle) cell, the method comprising providing said cell with a molecule that binds to a continuous stretch of at least 21 nucleotides within said exon.
