您的位置: 首页 > 农业专利 > 详情页

METHODS AND MEANS FOR EFFICIENT SKIPPING OF EXON 45 IN DUCHENNE MUSCULAR DYSTROPHY PRE-mRNA
专利权人:
JOSEPHUS JOHANNES DE KIMPE;ANNEMIEKE AARTSMA-RUS;GERARDUS JOHANNES PLATENBURG;JUDITH CHRISTINA THEODORA VAN DEUTEKOM;GARRIT-JAN BOUDEWIJN VAN OMMEN
发明人:
JOSEPHUS JOHANNES DE KIMPE,GERARDUS JOHANNES PLATENBURG,JUDITH CHRISTINA THEODORA VAN DEUTEKOM,ANNEMIEKE AARTSMA-RUS,GARRIT-JAN BOUDEWIJN VAN OMMEN
申请号:
US13094548
公开号:
US20120022134A1
申请日:
2011.04.26
申请国别(地区):
US
年份:
2012
代理人:
摘要:
The invention relates to a method for inducing or promoting skipping of exon 45 of DMD pre-mRNA in a Duchenne Muscular Dystrophy patient, preferably in an isolated (muscle) cell, the method comprising providing said cell with a molecule that binds to a continuous stretch of at least 21 nucleotides within said exon. The invention further relates to such molecule used in said method.
来源网站:
中国工程科技知识中心
来源网址:
http://www.ckcest.cn/home/

意 见 箱

匿名:登录

个人用户登录

找回密码

第三方账号登录

忘记密码

个人用户注册

必须为有效邮箱
6~16位数字与字母组合
6~16位数字与字母组合
请输入正确的手机号码

信息补充