ANNEMIEKE AARTSMA-RUS;JOSEPHUS JOHANNES DE KIMPE;ACADEMISCH ZIEKENHUIS LEIDEN;PROSENSA B.V.;PROSENSA TECHNOLOGIES B.V.;JUDITH CHRISTINA THEODORA VAN DEUTEKOM;GARRIT-JAN BOUDEWIJN VAN OMMEN;PROSENSA HO
发明人:
JUDITH CHRISTINA THEODORA VAN DEUTEKOM,ANNEMIEKE AARTSMA-RUS,JOSEPHUS JOHANNES DE KIMPE,GARRIT-JAN BOUDEWIJN VAN OMMEN,GERADUS JOHANNES PLATENBURG
申请号：
IL21250811
公开号：
IL212508A
申请日:
2011.04.27
申请国别(地区):
IL
年份:
2013
代理人:
摘要：
The invention relates to a method for inducing or promoting skipping of exon 45 of DMD pre-mRNA in a Duchenne Muscular Dystrophy patient, preferably in an isolated (muscle) cell, the method comprising providing said cell with a molecule that binds to a continuous stretch of at least 21 nucleotides within said exon.
