REGENXBIO Inc.;Regents of the University of Minnesota
发明人:
申请号：
EP19202040.2
公开号：
EP3622821A1
申请日:
2014.05.15
申请国别(地区):
EP
年份:
2020
代理人:
摘要：
A method to prevent, inhibit or treat one or more symptoms associated with a disease of the central nervous system by intrathecally, intracerebroventricularly or endovascularly administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease.
