REGENXBIO INC.;REGENTS OF THE UNIVERSITY OF MINNESOTA
发明人:
MCIVOR, R. SCOTT,BELUR, LALITHA R.,KOZARSKY, KAREN
申请号：
CA2986252
公开号：
CA2986252A1
申请日:
2016.05.13
申请国别(地区):
CA
年份:
2016
代理人:
摘要：
A method to prevent, inhibit or treat one or more symptoms associated with disease of the central nervous system by intranasally, intrathecally, intracerebrovascularly or intravenously administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease, in an amount effective, e.g., to provide for cross-correction.
