MUELLER, Christian,ARONIN, Neil,PFISTER, Edith, L.
申请号：
PH12019500626
公开号：
PH12019500626A1
申请日:
2019.03.22
申请国别(地区):
PH
年份:
2019
代理人:
摘要：
Aspects of the disclosure relate to compositions and methods useful for treating Huntington' s disease. In some embodiments, the disclosure provides interfering nucleic acids (e.g., artificial miRNAs) targeting the huntingtin gene (HTT) and methods of treating Huntington's disease using the same.
