Regents of the University of Minnesota;RegenxBio Inc.
发明人:
McIvor, R. Scott,Belur, Lalitha R.,Low, Walter,Fairbanks, Carolyn,Kozarsky, Karen
申请号：
AU20180253615
公开号：
AU2018253615(A1)
申请日:
2018.10.26
申请国别(地区):
澳大利亚
年份:
2018
代理人:
摘要：
Abstract A method to prevent, inhibit or treat one or more symptoms associated with a disease of the central nervous system by intrathecally, intracerebroventricularly or endovascularly administering a rAAV 5 encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease.
