REGENXBIO Inc.;Regents of the University of Minnesota
发明人:
R. Scott McIvor,Lalitha R. Belur,Walter Low,Carolyn Fairbanks,Karen Kozarsky
申请号：
US16438143
公开号：
US20190298812A1
申请日:
2019.06.11
申请国别(地区):
US
年份:
2019
代理人:
摘要：
A method to prevent, inhibit or treat one or more symptoms associated with a disease of the central nervous system by intrathecally, intracerebroventricularly or endovascularly administering a rAAV encoding a gene product associated with the disease, e.g., a mammal in which the gene product is absent or present at a reduced level relative to a mammal without the disease.
