O'RIORDAN, Catherine R.,PALERMO, Adam,RICHARDS, Brenda,STANEK, Lisa M.
申请号：
AU2018335410
公开号：
AU2018335410A1
申请日:
2018.09.21
申请国别(地区):
AU
年份:
2020
代理人:
摘要：
Provided herein are RNAi molecules for treating Huntington' s disease. Further provided herein are expression cassettes, vectors (e.g., rAAV, recombinant adenoviral, recombinant lentiviral, and recombinant HSV vectors), cells, viral particles, and pharmaceutical compositions containing the RNAi. Yet further provided herein are methods and kits related to the use of the RNAi, for example, to treat Huntington's disease.
