THE UNIVERSITY OF NORTH CAROLINA AT CHAPEL HILL;北卡羅來納大學教堂山分校
发明人:
HIRSCH, Matthew Louis,SAMULSKI, Richard Jude,SAMULSKI, Richard Jude,R‧J‧薩穆爾斯基
申请号:
HK18114841
公开号:
HK1255692A1
申请日:
2018.11.20
申请国别(地区):
HK
年份:
2019
代理人:
摘要:
This invention relates to viral vectors for delivery of alpha-L-iduronidase to the cornea of a subject and methods of using the same for treatment and prevention of corneal clouding and blindness in a subject due to mucopolysaccharidosis I.