RESEARCH INSTITUTE AT NATIONWIDE CHILDREN'S HOSPITAL;RESEARCH INSTITUTE AT NATIONWIDE CHILDRENS HOSPITAL
发明人:
RODINO-KLAPAC, LOUISE,MENDELL, JERRY R.
申请号：
CA3020999
公开号：
CA3020999A1
申请日:
2017.04.14
申请国别(地区):
CA
年份:
2017
代理人:
摘要：
The invention provides for recombinant AAV vectors comprising a miniaturized human micro-dystrophin gene and methods of using the recombinant vectors to reduce or prevent fibrosis in subjects suffering from muscular dystrophy.
