BLANCHARD, JAN E.,BROWN, ERIC D.,TROPAK, MICHAEL B.,MAHURAN, DON J.,BUTTNER, JUSTIN D.
申请号：
CA2699864
公开号：
CA2699864C
申请日:
2008.09.16
申请国别(地区):
CA
年份:
2016
代理人:
摘要：
Therapeutic compositions and methods for treatment of late-onset Gaucherdisease are described herein. Thecompositions comprise compounds having activity as pharmacological chaperonesfor mutant forms of the beta-glucocerebrosidase.Methods of treatment involve providing therapeutically effective amounts ofsuch compositions to subjects in need thereof.
