Don J Mahuran,Michael B Tropak,Justin D Buttner,Jan E Blanchard,Eric D Brown
申请号：
US13676506
公开号：
US08951994B2
申请日:
2012.11.14
申请国别(地区):
US
年份:
2015
代理人:
摘要：
Therapeutic compositions and methods for treatment of late-onset Gaucher disease are described herein. The compositions comprise compounds having activity as pharmacological chaperones for mutant forms of the beta-glucocerebrosidase. Methods of treatment involve providing therapeutically effective amounts of such compositions to subjects in need thereof.
