Don J. Mahuran,Michael B. Tropak,Justin D. Buttner,Jan E. Blanchard,Eric D. Brown
申请号：
US13775388
公开号：
US20130184352A1
申请日:
2013.02.25
申请国别(地区):
US
年份:
2013
代理人:
摘要：
Therapeutic compositions and methods for treatment of late-onset Gaucher disease are described herein. The compositions comprise compounds having activity as pharmacological chaperones for mutant forms of the beta-glucocerebrosidase. Methods of treatment involve providing therapeutically effective amounts of such compositions to subjects in need thereof.
