KANJOLIA, Arti Mahendra Prakash,ODATE, Shobu,SEITZER, Jessica Lynn,LESCARBEAU, Reynald Michael,STRAPPS, Walter
申请号：
SG11202002565Y
公开号：
SG11202002565YA
申请日:
2018.09.28
申请国别(地区):
SG
年份:
2020
代理人:
摘要：
Compositions and methods for editing, e.g., introducing double-stranded breaks, within the TTR gene are provided. Compositions and methods for treating subjects having amyloidosis associated with transthyretin (ATTR), are provided.
