KANJOLIA, ARTI MAHENDRA PRAKASH,ODATE, SHOBU,SEITZER, JESSICA LYNN,LESCARBEAU, REYNALD MICHAEL,STRAPPS, WALTER
申请号：
CA3077251
公开号：
CA3077251A1
申请日:
2018.09.28
申请国别(地区):
CA
年份:
2019
代理人:
摘要：
Compositions and methods for editing, e.g., introducing double-stranded breaks, within the TTR gene are provided. Compositions and methods for treating subjects having amyloidosis associated with transthyretin (ATTR), are provided.
