Indiana University Research & Technology Corporation
发明人:
Androphy, Elliot J.,Cherry, Jonathon J.,Cuny, Gregory D.,Glicksman, Marcie A.
申请号:
AU2013289938
公开号:
AU2013289938A1
申请日:
2013.07.12
申请国别(地区):
AU
年份:
2015
代理人:
摘要:
Disclosed herein are compositions and methods for treatment of spinal muscular atrophy (SMA). In certain embodiments, compounds are provided that increase full-length survival of motor neuron (SMN) protein production by an