COMPOSITIONS FOR INCREASING SURVIVAL OF MOTOR NEURON PROTEIN (SMN) LEVELS IN TARGET CELLS AND METHODS OF USE THEREOF FOR THE TREATMENT OF SPINAL MUSCULAR ATROPHY

• 收藏
• 分享

专利权人:

发明人:

Megerditch KILEDJIAN,Mi ZHOU

申请号：

US15506917

公开号：

US20170355956A1

申请日:

2015.09.04

申请国别(地区):

US

年份:

2017

代理人:

摘要：

Compositions for altering splicing activity of the DcpS gene and increasing SMN protein expression in target cells are provided. Also disclosed are methods of use of such compositions for the treatment of SMA.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/