CENTRO DE INVESTIGACIONES ENERGETICAS; MEDIOAMBIENTALES Y TECNOLOGICAS
发明人:
SEGOVIA, JOSE C.,GOMEZ, MARIA G.,NAVARRO, SUSANA,MEZA, NESTOR,BUEREN, JUAN,BRAVO, MARIA G.
申请号:
CA3021572
公开号:
CA3021572A1
申请日:
2017.04.20
申请国别(地区):
CA
年份:
2017
代理人:
摘要:
The present disclosure provides polynucleotide cassettes, expression vectors and methods for the expression of a gene in mammalian cells to provide gene therapy for pyruvate kinase deficiency.