FUNDACION INSTITUTO DE INVESTIGACION SANITARIA FUNDACION JIMENEZ DIAZ; MEDIOAMBIENTALES Y TECNOLOGICAS;CENTRO DE INVESTIGACIONES ENERGETICAS, MEDIOAMBIENTALES Y TECNOLOGICAS;CENTRO DE INVESTIGACIONES ENERGETICAS;CENTRO DE INVESTIGACION BIOMEDICA EN RED
发明人:
SEGOVIA, Jose C.,GOMEZ, Maria G.,NAVARRO, Susana,MEZA, Nestor,BUEREN, Juan,BRAVO, Maria G.
申请号:
SG11201809096V
公开号:
SG11201809096VA
申请日:
2017.04.20
申请国别(地区):
SG
年份:
2018
代理人:
摘要:
The present disclosure provides polynucleotide cassettes, expression vectors and methods for the expression of a gene in mammalian cells to provide gene therapy for pyruvate kinase deficiency.