Bourque, Elyse,Cabrera-Salazar, Mario A.,Celatka, Cassandra,Cheng, Seng H.,Hirth, Bradford,Good, Andrew,Jancsics, Katherine,Marshall, John,Metz, Markus,Scheule, Ronald K.,Skerlj, Renato,Xiang, Yibin,Z
申请号:
AU2013315715
公开号:
AU2013315715A1
申请日:
2013.09.10
申请国别(地区):
AU
年份:
2015
代理人:
摘要:
The invention relates to inhibitors of glucosylceramide synthase (GCS) useful for the treatment of metabolic diseases, such as lysosomal storage diseases, either alone or in combination with enzyme replacement therapy, cystic disease and for the treatment of cancer.