JOHN P. LEONARD,JEAN-FRANÇOIS DELEUZE,JEAN-MICHEL ITIER,CÉCILE ORSINI,GWÉNAËLLE RET-LECUELLE,SANDRA VIALE
申请号：
US15108686
公开号：
US20160361301A1
申请日:
2014.12.09
申请国别(地区):
US
年份:
2016
代理人:
摘要：
The invention relates to inhibitors of glucosylceramide synthase (GCS) useful for the treatment metabolic diseases, such as lysosomal storage diseases, either alone or in combination with enzyme replacement therapy.
